KH631: A Gene Therapy Product

Gene therapy is an emerging treatment approach which is designed to introduce foreign genetic material into target cells, to correct or compensate for genetic defects and abnormalities so as to treat diseases.

In the past few years, an increasing volume of mature data has been obtained from clinical trials in the fields of genome editing and gene therapy, demonstrating the efficacy and safety of gene therapy for a range of severe diseases in humans.

As an ideal treatment for patients with eye diseases, KH631 can produce longer durations of drug actions and require less frequent dosing.

*This is in clinical trials